Term Name: orphan drug
Synonyms: orphan drugs
Definition: Any drug that has been developed specifically for treatment of a rare medical condition, the condition itself being known as an orphan disease.
Ontology: ChEBI [CHEBI:71031]  ( EBI )

Relationships
is a type of: drug
inverse has_role: 4-aminopyridine ACT-333679 carglumic acid isavuconazole isavuconazonium sulfate ivacaftor ixazomib ixazomib citrate lenvatinib lenvatinib mesylate lumacaftor macitentan Orkambi rifaximin selexipag sodium phenylbutyrate uridine triacetate